Muscle Gene Therapy Methods and Protocols /
Gene therapy offers many conceptual advantages to treat muscle diseases, especially various forms of muscular dystrophies; however, it faces a number of unique challenges, including the need to deliver a therapeutic vector to all muscles throughout the body. In Muscle Gene Therapy: Methods and Proto...
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| Natura: | Elettronico eBook |
| Lingua: | English |
| Pubblicazione: |
Totowa, NJ :
Humana Press : Imprint: Humana,
2011.
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| Edizione: | 1st ed. 2011. |
| Serie: | Methods in Molecular Biology,
709 |
| Soggetti: | |
| Accesso online: | https://doi.org/10.1007/978-1-61737-982-6 |
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Sommario:
- Design and Testing of Regulatory Cassettes for Optimal Activity in Skeletal and Cardiac Muscle
- Codon Optimization of the Micro-Dystrophin Gene for Duchene Muscular Dystrophy Gene Therapy
- Monitoring Duchenne Muscular Dystrophy Gene Therapy with Epitope-Specific Monoclonal Antibodies
- Methods for Non-Invasive Monitoring of Muscle Fiber Survival with an AAV Vector Encoding the mSEAP Reporter Gene
- Monitoring Murine Skeletal Muscle Function for Muscle Gene Therapy
- Phenotyping Cardiac Gene Therapy in Mice
- Golden Retriever Muscular Dystrophy (GRMD): Developing and Maintaining a Colony and Physiological Functional Measurements
- Directed Evolution of Adeno-Associated Virus (AAV) as Vector for Muscle Gene Therapy
- Systemic Gene Transfer to Skeletal Muscle Using Reengineered AAV Vectors
- Bioinformatic and Functional Optimization of Antisense Phosphorodiamidate Morpholino Oligomers (PMOs) for Therapeutic Modulation of RNA Splicing in Muscle
- Engineering Exon-Skipping Vectors Expressing U7snRNA Constructs for Duchenne Muscular Dystrophy Gene Therapy
- Application of MicroRNA in Cardiac and Skeletal Muscle Disease Gene Therapy
- Molecular Imaging of RNA Interference Therapy Targeting PHD2 for Treatment of Myocardial Ischemia
- Lentiviral Vector Delivery of shRNA into Cultured Primary Myogenic Cells: A Tool for Therapeutic Target Validation
- Fetal Muscle Gene Therapy/Gene Delivery in Large Animals
- Electroporation of Plasmid DNA to Swine Muscle
- Local Gene Delivery and Methods to Control Immune Responses in Muscles of Normal and Dystrophic Dogs
- Gene Transfer to Muscle from the Isolated Regional Circulation
- AAV-Mediated Gene Therapy to the Isolated Limb in Rhesus Macaques
- Antisense Oligo-Mediated Multiple Exon-Skipping in a Dog Model of Duchenne Muscular Dystrophy
- Whole Body Skeletal Muscle Transduction in Neonatal Dogs with AAV-9
- A Translatable, Closed Recirculation System for AAV6 Vector-Mediated Myocardial Gene Delivery in the Large Animal
- Method of Gene Delivery in Large Animal Models of Cardiovascular Diseases
- Percutaneous Transendocardial Delivery of Self-Complementary Adeno-Associated Virus 6 in the Canine.